For an up-to-date list of current UK based trials taking place visit Be Part of Research (resource provided by the National Institute for Health Research).
For an international search visit Clinical Trials (resource provided by the U.S. National Library of Medicine). This resource provides information on trial status including recruiting, completed or withdrawn and worldwide trial locations.
For a list of active research studies recruiting individuals with inherited metabolic disease in the UK download a spreadsheet from the BIMDG website.
To find out more about past or current trials speak to your doctor and learn about the risks and potential benefits.
A clinical trial is a research study involving people. A clinical trial is designed to carefully assess the safety and effectiveness of an investigational drug, device or method of treatment that has not yet been approved by a regulatory agency such as the U.S. Food and Drug Administration (FDA) or the European Medicines Agency (EMA). Carefully conducted clinical trials determine if a treatment works without too many side effects. Without the patients who volunteer to participate in clinical trials, the development of new medicines would not be possible.
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