Consent

This site uses third party services that need your consent. Learn more

Functional First party cookies needed for the website to function. These can't be turned off. Analytics Storage (like third party cookies) used for analytics. Ads & tracking Storage (like third party cookies) used for advertisement.

Video published on 15 November 2019

Gene Therapy for MPS by Derralynn Hughes

MPS National Conference 2019 Gene Therapy for MPS by Derralynn Hughes Lysosomal Storage Disorders Unit, Royal Free London NHS Foundation Trust, University College London

Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Gene Therapy for MPS by Derralynn Hughes

More videos

Fabry disease - Neurology update by Mark Roberts

Fabry Disease - What to look for in children by Anupam Chakrapani

Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

Family tree and the role of the genetic counsellors in metabolic MDT clinics by Dr Karolina Stepien

Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

Thank you, we received your message and will contact you as soon as possible.

Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

More videos

Fabry disease - Neurology update by Mark Roberts

Fabry Disease - What to look for in children by Anupam Chakrapani

Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

Family tree and the role of the genetic counsellors in metabolic MDT clinics by Dr Karolina Stepien

Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

Please fix the following problems with the form:

Thank you, we received your message and will contact you as soon as possible.