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Video published on 25 October 2019

Small molecules and scissors; an overview of current treatments and latest trial results

MPS National Conference 2019 Small molecules and scissors; current treatments and latest trial results by Dr Maureen Cleary Consultant Metabolic Paediatrician at Great Ormond St Hospital

Small molecules and scissors; an overview of current treatments and latest trial results by Dr Maureen Cleary

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Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Small molecules and scissors; an overview of current treatments and latest trial results

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Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

More videos

Gene therapy; where are we up to, what's currently happening

How the world of digital may help us to better understand impact of disease for patients

How your information can lead to future treatments

Importance of Sleep Studies

Managing difficult behaviour

Radiological Abnormalities in the skull and spine for MPS I

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