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AVROBIO announce collaborative research agreement with Manchester university for MPS II gene therapy

AVROBIO announce collaborative research agreement with Manchester university for MPS II gene therapy.

04/10/2020

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REGENXBIO announces expansion of gene therapy programme for the treatment of MPS II

REGENXBIO have released an update on the progress of their investigational gene therapy programme for MPS II Hunters disease.

02/10/2020

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Brain disease treatment shows promising signs

Early results for a potentially revolutionary brain disease therapy given under compassionate use to a two-year-old has shown promise.

14/05/2020

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Vimizim re-evaluation process suspended - NICE's statement and MPS Society's response

NICE have today (28 February 2020) released the following statement in regards to the re-evaluation of Vimizim under the terms of the MAA.

28/02/2020