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Video published on 15 November 2019

Gene therapy for MPS? by Derralynn A Hughes

Focus on Fabry - Expert and Patient Meeting 2019 Gene therapy for MPS? by Derralynn A Hughes Lysosomal Storage Disorders Unit, Royal Free London NHS Foundation Trust

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Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Gene therapy for MPS? by Derralynn A Hughes

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Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

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Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

Gene Therapy for MPS by Derralynn Hughes

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Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

More videos

Fabry Disease - What to look for in children by Anupam Chakrapani

Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

Family tree and the role of the genetic counsellors in metabolic MDT clinics by Dr Karolina Stepien

Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

Gene Therapy for MPS by Derralynn Hughes

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