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Video published on 15 November 2019

New therapies for Fabry disease by Derralynn Hughes

Focus on Fabry - Expert and Patient Meeting 2019 New therapies for Fabry disease by Derralynn A Hughes Lysosomal Storage Disorders Unit, Royal Free London NHS Foundation Trust

New therapies for Fabry disease by Derralynn A Hughes

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Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

New therapies for Fabry disease by Derralynn Hughes

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Thank you, we received your message and will contact you as soon as possible.

Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

More videos

How are drugs approved and audited? by Tom Kenny

How the Fabry app can help clinicians to better understand pain in Fabry disease by Uma Ramaswami

How your information can lead to future treatments by Jacqueline Adam

Moving to Semi or Full independence for ERT infusions by Catherine Stewart

MPS Cardiac Masterclass

Mutations and predictions of disease severity by Derralynn Hughes

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