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Video published on 15 November 2019

How are drugs approved and audited? by Tom Kenny

Focus on Fabry - Expert and Patient Meeting 2019 How are drugs approved and audited? by Tom Kenny Role of CRG, NHSE and NICE

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Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

How are drugs approved and audited? by Tom Kenny

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Consent

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

Now is the time: global unity for rare disease progress

MPS Awareness Day event a success

Contact us

Make a difference

More videos

Fabry diseases - What causes my symptoms? by Dr Ana Janovic and Mark Roberts

Fabry in Families by Jacqueline Adam

Family tree and the role of the genetic counsellors in metabolic MDT clinics by Dr Karolina Stepien

Gap year, "Uni" and Transition - Anything is possible by Louis Garthwaite

Gene Therapy for MPS by Derralynn Hughes

Gene therapy for MPS? by Derralynn A Hughes

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